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A curated list of Natural Language Processing (NLP) research papers in the field of Evidence-Based Medicine (EBM).

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Awesome - Natural Language Processing in Support of Evidence-based Medicine

Awesome

A curated list of Natural Language Processing (NLP) research papers in the field of Evidence-Based Medicine (EBM).

This list is based on the scoping review “Natural Language Processing in Support of Evidence-Based Medicine: A Scoping Review” (ACL 2025 submission), which surveyed 129 peer-reviewed publications from 2019–2024.

The growth of medical literature demands automated tools to support clinicians in searching, appraising, synthesizing, and applying evidence in clinical practice. NLP is at the core of this transformation.

Table of Contents

NLP techniques for EBM

1. Ask – Search and Question Formulation

Here is the Markdown table ordered by year (from latest to earliest):

Paper Venue Date
The Use of Generative AI for Scientific Literature Searches for Systematic Reviews: ChatGPT and Microsoft Bing AI Performance Evaluation JMIR Med Inform 2024
Matching patients to clinical trials with large language models Nat Commun 2024
A span-based model for extracting overlapping PICO entities from randomized controlled trial publications J Am Med Inform Assoc 2024
LeafAI: query generator for clinical cohort discovery rivaling a human programmer J Am Med Inform Assoc 2023
Deep learning to refine the identification of high-quality clinical research articles from the biomedical literature: Performance evaluation J Biomed Inform 2023
ScanMedicine: An online search system for medical innovation Contemp Clin Trials 2023
Automatically Summarizing Evidence from Clinical Trials: A Prototype Highlighting Current Challenges ACL 2023
Investigation into Scaling-Up the SOAP Problem-Oriented Medical Record into a Clinical Case Study ICHI 2023
In a pilot study, automated real-time systematic review updates were feasible, accurate, and work-saving J Clin Epidemiol 2023
In Silico Drug Repurposing using Knowledge Graph Embeddings for Alzheimer's Disease ICBRA 2022
State-of-the-Art Evidence Retriever for Precision Medicine: Algorithm Development and Validation JMIR Med Inform 2022
Trial2Vec: Zero-Shot Clinical Trial Document Similarity Search using Self-Supervision EMNLP 2022
Cohort-based Clinical Trial Retrieval ADCS 2022
Improvement of intervention information detection for automated clinical literature screening during systematic review J Biomed Inform 2022
Preliminary Comparison of the Performance of the National Library of Medicine's Systematic Review Publication Type and the Sensitive Clinical Queries Filter for Systematic Reviews in PubMed JMLA 2022
COVID-19 trial graph: a linked graph for COVID-19 clinical trials J Am Med Inform Assoc 2021
Automate clinical evidence synthesis by linking trials to publications with text analytics ISEEIE 2021
A probabilistic precision information retrieval model for personalized clinical trial recommendation based on heterogeneous data ICCCNT 2021
Precision Medicine Search for Paediatric Oncology SIGIR 2021
Evaluation of Applied Machine Learning for Health Misinformation Detection via Survey of Medical Professionals on Controversial Topics in Pediatrics ICMHI 2021
Matching patients to clinical trials using semantically enriched document representation J Biomed Inform 2020
Natural Language Processing for Mimicking Clinical Trial Recruitment in Critical Care: A Semi-Automated Simulation Based on the LeoPARDS Trial IEEE J Biomed Health Inform 2020
Clinical trial search: Using biomedical language understanding models for re-ranking J Biomed Inform 2020
A2A: a platform for research in biomedical literature search BMC Bioinformatics 2020
DQueST: dynamic questionnaire for search of clinical trials J Am Med Inform Assoc 2019
Linking Knowledge Discovery In Clinical Notes And Massive Biomedical Literature Repositories BIBM 2019
An Experimentation Platform for Precision Medicine SIGIR 2019

2. Acquire – Extracting Evidence

Entity Extraction and Normalization

Paper Venue Date
Automatic categorization of self-acknowledged limitations in randomized controlled trial publications J Biomed Inform 2024
Utilizing Large Language Models for Enhanced Clinical Trial Matching: A Study on Automation in Patient Screening Cureus 2024
AutoCriteria: a generalizable clinical trial eligibility criteria extraction system powered by large language models J Am Med Inform Assoc 2024
Automating Clinical Trial Eligibility Screening: Quantitative Analysis of GPT Models versus Human Expertise PETRA 2024
Matching Patients to Accelerate Clinical Trials (MPACT): Enabling Technology for Oncology Clinical Trial Workflow Stud Health Technol Inform 2024
The Use of Generative AI for Scientific Literature Searches for Systematic Reviews: ChatGPT and Microsoft Bing AI Performance Evaluation JMIR Med Inform 2024
AlpaPICO: Extraction of PICO frames from clinical trial documents using LLMs Methods 2024
BLINKtextsubscriptLSTM: BioLinkBERT and LSTM based approach for extraction of PICO frame from Clinical Trial Text CODS-COMAD 2024
PICO to PICOS: Weak Supervision to Extend Datasets with New Labels Stud Health Technol Inform 2024
TCGA-Reports: A machine-readable pathology report resource for benchmarking text-based AI models Patterns 2024
Optimizing Clinical Trial Eligibility Design Using Natural Language Processing Models and Real-World Data: Algorithm Development and Validation JMIR Med Inform 2024
Generative AI for evidence-based medicine: A PICO GenAI for Synthesizing Clinical Case Reports ICC 2024
Not so weak PICO:leveraging weak supervision for participants, interventions, and outcomes recognition for systematic review automatio J Am Med Inform Assoc Open 2023
LeafAI: query generator for clinical cohort discovery rivaling a human programmer J Am Med Inform Assoc 2023
Automatic knowledge graph population with model-complete text comprehension for pre-clinical outcomes in the field of spinal cord injury Artif Intell Med 2023
Towards precise PICO extraction from abstracts of randomized controlled trials using a section-specific learning approach Bioinformatics 2023
EvidenceMap:a three-level knowledge representation for medical evidence computation and comprehension J Am Med Inform Assoc 2023
Automated Matching of Patients to Clinical Trials: A Patient-Centric Natural Language Processing Approach for Pediatric Leukemia JCO Clin Cancer Inform 2023
In a pilot study, automated real-time systematic review updates were feasible, accurate, and work-saving J Clin Epidemiol 2023
Parsable Clinical Trial Eligibility Criteria Representation Using Natural Language Processing AMIA 2023
Piloting an automated clinical trial eligibility surveillance and provider alert system based on artificial intelligence and standard data models BMC Med Res Methodol 2023
Controversial Trials First: Identifying Disagreement Between Clinical Guidelines and New Evidence AMIA 2022
In Silico Drug Repurposing using Knowledge Graph Embeddings ICBRA 2022
The Leaf Clinical Trials Corpus: a new resource for query generation from clinical trial eligibility criteria Sci Data 2022
Exploration of biomedical knowledge for recurrent glioblastoma using natural language processing deep learning models BMC Med Inform Decis Mak 2022
Implementation of Machine Learning Pipelines for Clinical Practice: Development and Validation Study JMIR Med Inform 2022
A comparative study of pre-trained language models for named entity recognition in clinical trial eligibility criteria from multiple corpora BMC Med Inform Decis Mak 2022
Evaluation of Criteria2Query: Towards Augmented Intelligence for Cohort Identification Stud Health Technol Inform 2022
Improvement of intervention information detection for automated clinical literature screening during systematic review J Biomed Inform 2022
srBERT: automatic article classification model for systematic review using BERT Syst Rev 2021
Creating and evaluating chatbots as eligibility assistants for clinical trials ACM Transactions on Computing for Healthcare 2021
Developing a fully automated evidence synthesis tool for identifying, assessing and collating the evidence BMJ Evid Based Med 2021
MSˆ2: Multi-Document Summarization of Medical Studies EMNLP 2021
UMLS-based data augmentation for natural language processing of clinical research literature J Am Med Inform Assoc 2021
Precision Medicine Search for Paediatric Oncology SIGIR 2021
Data Mining of Free-Text Responses: An Innovative Approach to Analyzing Patient Perspectives on Treatment for Chronic Rhinosinusitis with Nasal Polyps in a Phase IIa Proof-of-Concept Study for Dupilumab Patient Preference and Adherence 2021
A knowledge base of clinical trial eligibility criteria J Biomed Inform 2021
Evaluation of an artificial intelligence clinical trial matching system in Australian lung cancer patients J Am Med Inform Assoc Open 2020
Artificial intelligence tool for optimizing eligibility screening for clinical trials in a large community cancer center JCO Clin Cancer Inform 2020
Machine Learning Assisted Citation Screening for Systematic Reviews Stud Health Technol Inform 2020
The anatomy of the SARS-CoV-2 biomedical literature JMIR Med Inform 2020
Matching patients to clinical trials using semantically enriched document representation J Biomed Inform 2020
Clinical trial search: Using biomedical language understanding models for re-ranking J Biomed Inform 2020
Natural Language Processing for Mimicking Clinical Trial Recruitment in Critical Care IEEE J Biomed Health Inform 2020
Improving Disease Named Entity Recognition for Clinical Trial Matching BIBM 2019
Linking Knowledge Discovery In Clinical Notes And Massive Biomedical Literature Repositories BIBM 2019
Improving reference prioritisation with PICO recognition BMC Med Inform Decis Mak 2019
An approach for transgender population information extraction and summarization from clinical trial text BMC Med Inform Decis Mak 2019
Medical Knowledge Infused Convolutional Neural Networks for Cohort Selection in Clinical Trials J Am Med Inform Assoc 2019
Clinical trial cohort selection based on multi-level rule-based natural language processing system J Am Med Inform Assoc 2019
Extractive summarization of clinical trial descriptions Int J Med Inform 2019
Pretraining to recognize PICO Elements from Randomized Controlled Trial Literature Stud Health Technol Inform 2019
DQueST: dynamic questionnaire for search of clinical trials J Am Med Inform Assoc 2019
Data-driven method to enhance craniofacial and oral phenotype vocabularies J Am Dent Assoc 2019
Impact of size, location, symptomatic-nature and gender on the rupture of saccular intracranial aneurysms ASONAM 2018

Relation Extraction

Paper Venue Date
AutoTrial: Prompting Language Models for Clinical Trial Design EMNLP 2023
LeafAI: query generator for clinical cohort discovery rivaling a human programmer J Am Med Inform Assoc 2023
Controversial Trials First: Identifying Disagreement Between Clinical Guidelines and New Evidence AMIA 2022
The Leaf Clinical Trials Corpus: a new resource for query generation from clinical trial eligibility criteria Sci Data 2022
Evaluation of Criteria2Query: Towards Augmented Intelligence for Cohort Identification MedInfo 2022
Knowledge graph based platform of COVID-19 drugs and symptoms ASONAM 2021
Enhancing evidence-based medicine with natural language argumentative analysis of clinical trials Artif Intell Med 2021
A knowledge base of clinical trial eligibility criteria J Biomed Inform 2021
MS²: Multi-Document Summarization of Medical Studies EMNLP 2021
srBERT: automatic article classification model for systematic review using BERT Syst Rev 2021
Linking Knowledge Discovery In Clinical Notes And Massive Biomedical Literature Repositories BIBM 2019
An approach for transgender population information extraction and summarization from clinical trial text BMC Med Inform Decis Mak 2019

3. Appraise, Synthesize, and Summarization

Quality Assessment

Paper Venue Date
Automatic categorization of self-acknowledged limitations in randomized controlled trial publications J Biomed Inform 2024
Utilizing ChatGPT as a scientific reasoning engine to differentiate conflicting evidence and summarize challenges in controversial clinical questions J Am Med Inform Assoc 2024
Deep learning to refine the identification of high-quality clinical research articles from the biomedical literature: Performance evaluation J Biomed Inform 2023
OncoCTMiner: streamlining precision oncology trial matching via molecular profile analysis Database (Oxford) 2023
The Use of Generative AI for Scientific Literature Searches for Systematic Reviews: ChatGPT and Microsoft Bing AI Performance Evaluation JMIR Med Inform 2024
State-of-the-Art Evidence Retriever for Precision Medicine: Algorithm Development and Validation JMIR Med Inform 2022
Validating GAN-BioBERT: A Methodology for Assessing Reporting Trends in Clinical Trials Front Digit Health 2022
Transformer-based named entity recognition for parsing clinical trial eligibility criteria BCB 2021
Developing a fully automated evidence synthesis tool for identifying, assessing and collating the evidence BMJ Evid Based Med 2021
Towards Automated Detection of Contradictory Research Claims in Medical Literature Using Deep Learning Approach CAMP 2021
Machine Learning Assisted Citation Screening for Systematic Reviews Stud Health Technol Inform 2020

Evidence Ranking and Screening

Paper Venue Date
AutoCriteria: a generalizable clinical trial eligibility criteria extraction system powered by large language models J Am Med Inform Assoc 2024
Towards autonomous living meta-analyses: A framework for automation of systematic review and meta-analyses Stud Health Technol Inform 2024
Matching patients to clinical trials with large language models Nat Commun 2024
Using artificial intelligence to identify drugs for repurposing to treat l-DOPA induced dyskinesia Neuropharmacology 2024
OncoCTMiner: streamlining precision oncology trial matching via molecular profile analysis Database (Oxford) 2023
Piloting an automated clinical trial eligibility surveillance and provider alert system based on artificial intelligence and standard data models BMC Med Res Methodol 2023
Preliminary Comparison of the Performance of the National Library of Medicine's Systematic Review Publication Type and the Sensitive Clinical Queries Filter for Systematic Reviews in PubMed J Med Libr Assoc 2022
Cohort-based Clinical Trial Retrieval ADCS 2022
srBERT: automatic article classification model for systematic review using BERT Syst Rev 2021
Automate clinical evidence synthesis by linking trials to publications with text analytics ISEEIE 2021
A probabilistic precision information retrieval model for personalized clinical trial recommendation based on heterogeneous data ICCCNT 2021
Artificial intelligence clinical evidence engine for automatic identification, prioritization, and extraction of relevant clinical oncology research JCO Clin Cancer Inform 2021
The anatomy of the SARS-CoV-2 biomedical literature: Introducing the CovidX network algorithm for drug repurposing recommendation JMIR Med Inform 2020
Clinical trial search: Using biomedical language understanding models for re-ranking J Biomed Inform 2020
Improving reference prioritisation with PICO recognition BMC Med Inform Decis Mak 2019
An Experimentation Platform for Precision Medicine SIGIR 2019
Measuring the impact of screening automation on meta-analyses of diagnostic test accuracy Syst Rev 2019

Evidence Synthesis

Paper Venue Date
Utilizing ChatGPT as a scientific reasoning engine to differentiate conflicting evidence and summarize challenges in controversial clinical questions J Am Med Inform Assoc 2024
Generative AI for evidence-based medicine: A PICO GenAI for synthesizing clinical case reports ICC 2024
Towards autonomous living meta-analyses: A framework for automation of systematic review and meta-analyses Stud Health Technol Inform 2024
In a pilot study, automated real-time systematic review updates were feasible, accurate, and work-saving J Clin Epidemiol 2023
Automatic knowledge graph population with model-complete text comprehension for pre-clinical outcomes in the field of spinal cord injury Artif Intell Med 2023
EvidenceMap: a three-level knowledge representation for medical evidence computation and comprehension J Am Med Inform Assoc 2023
AutoTrial: Prompting Language Models for Clinical Trial Design EMNLP 2023
Automatic data extraction to support meta-analysis statistical analysis: a case study on breast cancer BMC Med Inform Decis Mak 2022
Developing a fully automated evidence synthesis tool for identifying, assessing and collating the evidence BMJ Evid Based Med 2021
Machine Learning Assisted Citation Screening for Systematic Reviews Stud Health Technol Inform 2020

Evidence Summarization

Paper Venue Date
TriSum: Learning summarization ability from large language models with structured rationale NAACL 2024
Utilizing ChatGPT as a scientific reasoning engine to differentiate conflicting evidence and summarize challenges in controversial clinical questions J Am Med Inform Assoc 2024
Automatically Summarizing Evidence from Clinical Trials: A Prototype Highlighting Current Challenges ACL 2023
Exploring ChatGPT's potential in facilitating adaptation of clinical guidelines: A case study of Diabetic Ketoacidosis guidelines Cureus 2023
EvidenceMap: a three-level knowledge representation for medical evidence computation and comprehension J Am Med Inform Assoc 2023
Text summarization of medical documents using abstractive techniques ICAAIC 2023
Integrating a PICO clinical questioning to the QL4POMR framework for building evidence-based clinical case reports IEEE Big Data 2023
Pre-trained language models with domain knowledge for biomedical extractive summarization Knowledge-Based Systems 2022
MSˆ2: Multi-Document Summarization of Medical Studies EMNLP 2021
Knowledge graph based platform of COVID-19 drugs and symptoms ASONAM 2021
A light-weight text summarization system for fast access to medical evidence Front Digit Health 2020
An approach for transgender population information extraction and summarization from clinical trial text BMC Med Inform Decis Mak 2019
Extractive summarization of clinical trial descriptions Int J Med Inform 2019

4. Apply & Assess – Adoption, refinement and research

Clinical Trial design and identification

Paper Venue Date
Utilizing Large Language Models for Enhanced Clinical Trial Matching: A Study on Automation in Patient Screening Cureus 2024
Natural language processing for adjudication of heart failure in a multicenter clinical trial: A secondary analysis of a randomized clinical trial JAMA Cardiology 2024
Automating clinical trial eligibility screening: Quantitative analysis of GPT Models versus Human Expertise PETRA 2024
Matching Patients to Accelerate Clinical Trials (MPACT) Enabling Technology for Oncology Clinical Trial Workflow Stud Health Technol Inform 2024
Optimizing Clinical Trial Eligibility Design Using Natural Language Processing Models and Real-World Data: Algorithm Development and Validation JMIR Med Inform 2024
Automating clinical trial matches via natural language processing of synthetic electronic health records and clinical trial eligibility criteria AMIA 2024
Distilling large language models for matching patients to clinical trials J Am Med Inform Assoc 2024
Matching patients to clinical trials with large language models Nat Commun 2024
Text classification of cancer clinical trial eligibility criteria AMIA 2024
Large Language Models for Healthcare Data Augmentation: An Example on Patient-Trial Matching AMIA 2024
LeafAI: query generator for clinical cohort discovery rivaling a human programmer J Am Med Inform Assoc 2023
Automatic knowledge graph population with model-complete text comprehension for pre-clinical outcomes in the field of spinal cord injury Artif Intell Med 2023
Automated Matching of Patients to Clinical Trials: A Patient-Centric Natural Language Processing Approach for Pediatric Leukemia JCO Clin Cancer Inform 2023
Parsable Clinical Trial Eligibility Criteria Representation Using Natural Language Processing AMIA 2023
Piloting an automated clinical trial eligibility surveillance and provider alert system based on artificial intelligence and standard data models BMC Med Res Methodol 2023
Parsing Clinical Trial Eligibility Criteria for Cohort Query by a Multi-Input Multi-Output Sequence Labeling Model BIBM 2023
Automatic Assessment of Patient Eligibility by Utilizing NLP and Rule-Based Analysis EMBC 2023
AutoTrial: Prompting Language Models for Clinical Trial Design EMNLP 2023
Implementation of Machine Learning Pipelines for Clinical Practice: Development and Validation Study JMIR Med Inform 2022
The Leaf Clinical Trials Corpus: a new resource for query generation from clinical trial eligibility criteria Sci Data 2022
Cohort-based Clinical Trial Retrieval ADCS 2022
A comparative study of pre-trained language models for named entity recognition in clinical trial eligibility criteria from multiple corpora BMC Med Inform Decis Mak 2022
Evaluation of Criteria2Query: Towards Augmented Intelligence for Cohort Identification Stud Health Technol Inform 2022
Improving the Efficiency of Clinical Trial Recruitment Using an Ensemble Machine Learning to Assist With Eligibility Screening ACR Open Rheumatology 2021
Creating and evaluating chatbots as eligibility assistants for clinical trials: An active deep learning approach towards user-centered classification ACM Transactions on Computing for Healthcare 2021
EMR2vec: Bridging the gap between patient data and clinical trial Comput Ind Eng 2021
A probabilistic precision information retrieval model for personalized clinical trial recommendation based on heterogeneous data ICCCNT 2021
A knowledge base of clinical trial eligibility criteria J Biomed Inform 2021
Transformer-based named entity recognition for parsing clinical trial eligibility criteria BCB 2021
Batch enrollment for an artificial intelligence-guided intervention to lower neurologic events in patients with undiagnosed atrial fibrillation: rationale and design of a digital clinical trial American Heart Journal 2021
Evaluation of an artificial intelligence clinical trial matching system in Australian lung cancer patients J Am Med Inform Assoc Open 2020
Artificial intelligence tool for optimizing eligibility screening for clinical trials in a large community cancer center JCO Clin Cancer Inform 2020
Matching patients to clinical trials using semantically enriched document representation J Biomed Inform 2020
Chia, a large annotated corpus of clinical trial eligibility criteria Sci Data 2020
Natural Language Processing for Mimicking Clinical Trial Recruitment in Critical Care: A Semi-Automated Simulation Based on the LeoPARDS Trial IEEE J Biomed Health Inform 2020
Improving Disease Named Entity Recognition for Clinical Trial Matching BIBM 2019
An approach for transgender population information extraction and summarization from clinical trial text BMC Med Inform Decis Mak 2019
Medical Knowledge Infused Convolutional Neural Networks for Cohort Selection in Clinical Trials J Am Med Inform Assoc 2019
Clinical trial cohort selection based on multi-level rule-based natural language processing system J Am Med Inform Assoc 2019
Cohort selection for clinical trials using deep learning models J Am Med Inform Assoc 2019
Cohort Selection for Clinical Trials From Longitudinal Patient Records: Text Mining Approach JMIR Med Inform 2019
Hybrid bag of approaches to characterize selection criteria for cohort identification J Am Med Inform Assoc 2019
A Real-Time Automated Patient Screening System for Clinical Trials Eligibility in an Emergency Department: Design and Evaluation JMIR Med Inform 2019

Question Answering

Paper Venue Date
Assessment of a Large Language Model's Responses to Questions and Cases About Glaucoma and Retina Management JAMA Ophthalmol 2024
TriSum: Learning summarization ability from large language models with structured rationale NAACL 2024
Generative AI for evidence-based medicine: A PICO GenAI for synthesizing clinical case reports ICC 2024
Performance of ChatGPT in Answering Clinical Questions on the Practical Guideline of Blepharoptosis Aesthetic Plast Surg 2024
Retrieval Augmented Generation enabled generative pre-trained transformer 4 (GPT-4) Performance for Clinical Trial Screening NEJM AI 2024
Development and evaluation of a large language model of ophthalmology in Chinese British Journal of Ophthalmology 2024
Aesthetic surgery advice and counseling from artificial intelligence: A rhinoplasty consultation with ChatGPT Aesthetic Plast Surg 2023
Exploring ChatGPT's potential in facilitating adaptation of clinical guidelines: A case study of Diabetic Ketoacidosis guidelines Cureus 2023
MediGPT: Exploring Potentials of Conventional and Large Language Models on Medical Data IEEE Access 2023
Exploration of biomedical knowledge for recurrent glioblastoma using natural language processing deep learning models BMC Med Inform Decis Mak 2022
Creating and evaluating chatbots as eligibility assistants for clinical trials: An active deep learning approach towards user-centered classification ACM Transactions on Computing for Healthcare 2021
Knowledge graph based platform of COVID-19 drugs and symptoms ASONAM 2021
MedTruth: A Semi-supervised Approach to Discovering Knowledge Condition Information from Multi-Source Medical Data CIKM 2019

Citation

If you find our work helpful, please cite the following.

Zihan Xu, Haotian Ma, Yihao Ding, Gongbo Zhang, Chunhua Weng, and Yifan Peng. 
2025. Natural Language Processing in Support of Evidence-based Medicine: A 
Scoping Review. In Findings of the Association for Computational Linguistics: 
ACL 2025, pages 21421–21443, Vienna, Austria. Association for Computational 
Linguistics.
@inproceedings{xu-etal-2025-natural,
    title = "Natural Language Processing in Support of Evidence-based Medicine: A Scoping Review",
    author = "Xu, Zihan  and
      Ma, Haotian  and
      Ding, Yihao  and
      Zhang, Gongbo  and
      Weng, Chunhua  and
      Peng, Yifan",
    booktitle = "Findings of the Association for Computational Linguistics: ACL 2025",
    month = jul,
    year = "2025",
    address = "Vienna, Austria",
    publisher = "Association for Computational Linguistics",
    url = "https://aclanthology.org/2025.findings-acl.1103/",
    pages = "21421--21443",
}

Acknowledgement

This project was sponsored by the National Library of Medicine grant R01LM009886, R01LM014344, and R01LM014573.

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A curated list of Natural Language Processing (NLP) research papers in the field of Evidence-Based Medicine (EBM).

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